KDA's Mission
The KDA is about to celebrate its 25th year. The KDA's mission has remained the same. To inform, support, educate, fund research and find a cure for Kennedy's Disease. Help us find a cure. Donate today
News & Events
AnnJi Pharmaceutical Company Announces Positive Phase 1/2a Results for AJ201 in Spinal and Bulbar Muscular Atrophy (SBMA) Patients.
Taipei, May 21, 2025 – AnnJi Pharmaceutical Co., Ltd., a clinical-stage Taiwanese biotechnology company focused on addressing unmet medical needs in dermatology, neurology, and rare diseases, today announced positive results from its Phase 1/2a randomized, double-blind, placebo-controlled, first-in-patient clinical trial of AJ201 in adults with Spinal and Bulbar Muscular Atrophy (SBMA). Conducted across six U.S. clinical sites, the study evaluated the safety, tolerability, pharmacokinetics (PK), and pharmacodynamics (PD) of AJ201 (ClinicalTrials.gov Identifier: NCT05517603). While not powered to assess efficacy, exploratory endpoints revealed meaningful treatment-related improvements that support continued clinical development. For more information, click here.
The 100-Step Challenge - Sign up today!
We’ve decided to recognize June as Kennedy’s Disease Awareness Month! While not officially designated, June holds special meaning as it coincides with Father’s Day, and many of those affected by Kennedy’s Disease are fathers and grandfathers who hope to find a cure for future generations. To mark the occasion, we invite you to take part in something meaningful: The 100-Step Challenge. Join us to help us find a cure for Kennedy's Disease, for more information, click here.
2025 Grants and Fellowship Announcement
The Kennedy's Disease Association is pleased to announce its 2025 SBMA research grants and fellowship programs. Through these programs, we seek to further understand the pathological mechanisms of and possible treatments for Kennedy's disease. For details and proposal instructions, click here. The submission deadline for both programs is Monday, June 2, 2025. Awards will be announced in September after a review by the KDA's Scientific Review Board.
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New research "Kennedy Disease in Latin America: Two New Mexican Cases and a Systematic Review of Regional Reports." To read the article, click here.
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Kennedy's Disease is an adult-onset disease with symptoms usually appearing between the ages of 30 and 50. However, earlier and later onsets have been recorded. Life expectancy is noted to be at or almost normal. Generally males with this inherited gene develop symptoms, while females with this gene are carriers. For more information click here.
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Kennedy's Disease support groups connect people living with and/or effected by Kennedy's Disease together for support. To find your group, click here.
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Need financial help to pay for the Kennedy's Disease DNA test. Use our Contact Us form by clicking here and add “DNA Test” to the subject line. We will send you an application form to be completed by your physician and yourself.
More News
Global Genes is a 501(c)(3) non-profit organization dedicated to eliminating the burdens and challenges of rare diseases for patients and families globally. The organization has many resources which include blog posts with information designed for people living with Rare Diseases like Kennedy's Disease. Subjects include: Global Genes Guide to Medical Gaslighting, Next Gen Advocacy and The Beginner’s Guide to Rare Disease.
The Kennedy's Disease Association supports the 2025 Gordon Research Conference (GRC). The CAG Triplet Repeat Disorders GRC is a premier, international scientific conference focused on advancing the frontiers of science through the presentation of cutting-edge and unpublished research, prioritizing time for discussion after each talk and fostering informal interactions among scientists of all career stages. The conference program includes a diverse range of speakers and discussion leaders from institutions and organizations worldwide, concentrating on the latest developments in the field. The conference is five days long and held in a remote location to increase the sense of camaraderie and create scientific communities, with lasting collaborations and friendships. To learn more, click here
Mr. Lewis Myers joins the Kennedy's Disease Association Board of Directors. Lewis brings a broad array of skills to the Kennedy’s Disease Association Board of Directors. To learn more about Lewis and other board members, click here.
